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Gene Therapy Normalizes the IgH Repertoire in ADA Deficiency

Description
Platforms
dbGaP
View in dbGaP
Summary
Consent CodesGRU-IRB-PUB-COL-NPU
Focus / DiseasesSevere combined immunodeficiency due to adenosine deaminase deficiency
Study DesignCase-Control
Data TypesRNA-Seq
Subjects40