Gene Therapy Normalizes the IgH Repertoire in ADA Deficiency

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Platforms
dbGaP
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Consent Codes

GRU-IRB-PUB-COL-NPU

Focus / Diseases

Severe combined immunodeficiency due to adenosine deaminase deficiency

Study Design

Case-Control

Data Types

RNA-Seq

Subjects

40
NCPI Dataset Catalog
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